Effectively Translate Complex Metabolic Gene Therapies
Into & Through the Clinic

More companies and institutions than ever before are embarking on development of gene therapies in metabolic disease, and they are encountering unique challenges, from fine-tuning dosing to defining clinically relevant biomarkers. Gene Therapy for Metabolic Disorders will unite large pharma and innovative biotechs to collectively overcome translational drug development barriers to deliver on the transformative promise of gene therapy approaches for patients in need. 

Incorporating in-depth insights into the leading metabolic disease programs, this event will ensure that you can optimize dosing to achieve the required enzyme levels without over-expression, define the necessary parameters for transitioning to first-in-human trials, and overcome unique challenges encountered in multi-organ systemic gene therapy delivery for complex metabolic indications. 

Don’t get left behind. Join colleagues from Preclinical, Translational and Clinical departments of leading companies including AVROBIO, Freeline Therapeutics and LogicBio to optimize your gene therapy approach and revolutionize the treatment of metabolic diseases. 

Register your interest for 2022 

Expert Speakers Include

Asif Paker

VP, Clinical Development

Swan Bio Therapeutics

Jingjing Jiang

Associate Director

Poseida Therapeutics

Kei Kishimoto

CSO

Selecta Biosciences

Rose Sheridan

VP,
Translational Research

Freeline Therapeutics

Cristina Baricordi

Senior Scientist

AVROBIO

Giuseppe Ronzitti

INSERM Researcher,
Head of Immunology and Liver Gene Transfer Laboratory

Genethon

Melanie Blank

Medical Officer,
Clinical Team Leader in OTAT

CBER

Michele Stone

VP,
Translational Development

Kriya Therapeutics

Attendees Of Other Gene Therapy Event Series Digital Meetings Have Said:

"It was very informative and
worked exceptionally well as a remote meeting." 

Novartis Gene Therapies 

 

“The event was a terrific overview of the gene therapy field, and was a great opportunity to see how other organizations view and address many relevant challenges.” 

Sarepta Therapeutics 

 

Other Events in the Gene Therapy Series